TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease
Por um escritor misterioso
Descrição
Children with Niemann-Pick Type C (NPC), their parents and scientists seeking a treatment for this fatal genetic disease. WSJ follows this 6-year fight.
Parents of kids with Niemann Pick C advocate for adrabetadex
Niemann-Pick Type C Disease - NP-C Genetic Disease - Lysosomal Disease
Save Purnell Today
Parents of twins with Niemann-Pick find a treatment
Twins with rare, fatal disease at center of multimillion-dollar lawsuit
Consensus clinical management guidelines for Niemann-Pick disease type C, Orphanet Journal of Rare Diseases
Experimental drug shows promise in cruel childhood disease
Efficacy and safety of arimoclomol in Niemann‐Pick disease type C: Results from a double‐blind, randomised, placebo‐controlled, multinational phase 2/3 trial of a novel treatment - Mengel - 2021 - Journal of Inherited
March 2022 – NNPDF
de
por adulto (o preço varia de acordo com o tamanho do grupo)
